Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A
Journal Article
Overview
publication date
- February 23, 2023
has subject area
- Biological Factors - Factor VIII
- Blood Coagulation Disorders - Hemophilia A
- Blood Proteins - Factor VIII
- Coagulation Protein Disorders - Hemophilia A
- Gene Transfer Techniques
- Genetic Diseases, Inborn - Hemophilia A
- Half-Life
- Hemorrhage
- Hemorrhagic Disorders - Hemophilia A
- Humans
- Male
- Protein Precursors - Factor VIII
- Recombinant Fusion Proteins
Date in CU Experts
- December 11, 2025 2:29 AM
Full Author List
- Mahlangu J; Kaczmarek R; von Drygalski A; Shapiro S; Chou S-C; Ozelo MC; Kenet G; Peyvandi F; Wang M; Madan B
author count
- 29
citation count
- 174
published in
- New England Journal of Medicine Journal
Other Profiles
International Standard Serial Number (ISSN)
- 0028-4793
Electronic International Standard Serial Number (EISSN)
- 1533-4406
Digital Object Identifier (DOI)
Additional Document Info
start page
- 694
end page
- 705
volume
- 388
issue
- 8